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The goal of gene therapy is to restore normal amounts of aspartoacylase in the brain and nervous system and prevent the build-up of NAA and the symptoms of Canavan disease
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Why is gene therapy a significant medical breakthrough?
Gene therapy is a significant medical breakthrough because it allows doctors to treat a disease before it becomes chronic or even reverse damage done by a chronic disease. It also allows for the treatment of diseases with no cure prior to gene therapy.
How could gene therapy be used to treat cancer?
With the help of Gene therapy we can replace or supress the cancer gene
Which type of disorder is most difficult to correct by gene therapy?
Gene Therapy cannot treat · Phenylketonuria · Gaucher Disease · Lesch-Nyhan Syndrome · Urea Cycle Disorders · Duchenne Muscular Dystrophy
What is the meaning of genetheraphy?
Gene therapy is when DNA is used to treat a disease. The DNA is placed into the patient's cells to help heal them of the illness that is present.
What is an example of a disease that might be treated using gene therapy?
It can be used to treat defects in somatic that is (body)or gametic (sperm or eggs) cell
What is cosmetic gene therapy?
Cosmetic gene therapy is a branch of medicine that deals with the maintenance and cure of the body disease.
How does gene therapy effect children?
Gene therapy effects children by helping to cure disease and to lengthen lives. Gene therapy can also be used to eliminate diseases that are inherited.
Is gene therapy available for Wilson's disease?
yes
How gene therapy might be used to treat cytic fibrosis?
In cystic fibrosis there is an inherited gene that you have that is causing it, so if gene therapy is used, you can replace the gene with the effected one
Which of the following is the first step in gene therapy?
Identifying the faulty Gene. Identifying the faulty Gene that causes the disease.
What is gene therapy?
Gene therapy is a method of treatment. It is specifically used to treat patients who are suffering from diseases due to defective genes. Essentially, the treatment involves researchers replacing the defective or faulty genes with a normal functioning gene. It involves: 1) Detection of gene 2)Determination & its role 3)Isolation & cloning 4)Introducing the gene by proper way. This is either germline gene therapy (done in germ cells) or somatic gene therapy (done in somatic cells).
What factors have kept gene therapy from becoming an effective treatment for genetic disease?
There are a number of factors which have kept gene therapy from becoming an effective treatment for genetic disease. The viral rectors are the main problems which might make gene therapy to cause diseases.
