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There is a treatment but no cure. Biomarin is developing an Enzyme Replacement Therapy for Morquio. They are expected to announce Phase 1/2 results shortly and from initial data (1mg/kg) efficacy and safety seem promising. If everything continues to look good a Phase 3 study could begin late '10/early '11 and if those results are positive the therapy could be on the market possibly as early as late '12. Getting into a Phase 3 trial would probably be the quickest way to get treatment though one could be randomized to Placebo. The possibility of compassionate use/early access exists as well. There was another company in earlier stages of development for an Enzyme Replacement but I believe they had (financial) problems.
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I had all the symptoms of Burning Mouth Syndrome. My family doctor prescribed a medicine used to treat the chicken pox virus (herpes). Thankfully all may symptoms went away wi…th no recurrence. What is interesting is that even though I have already had chicken pox when I was little, the BM symptoms began a few weeks after I had come in contact with a child who had chicken pox. This may be the reason for burning mouth syndrome knowing that the herpes virus effects the nerves in the mouth. It is worth asking your doctor about !!!!!
It is a genetic syndrome that makes it impossible to metabolize certain mucopolysaccharides. It cannot be prevented once born. It can be treated. The only way to prevent it i…s to use reproductive technology to make sure a child with it is not conceived.
The average height for someone with Morquios syndrome will grow an average of four feet. The life expectancy can vary from four years to seventy years.
Yes! Cowbell is the cure for peter pan syndrome. All you have to do is play the cowbell to the kid and their fish (if they don't have a fish get them one) and they will be cur…ed! This is not guaranteed and may have side effects including having an alliance with Captain Hook, crushing dreams FOREVER, and losing your love for cowbells and fish. I tried on my fish once, it died.
People get morquio's syndrome by inheriting it. Both sides of the family have to have. There mom and dad don't, but maybe a relative further down the line.
no, there is not a cure for WHS. Sadly but there are ways for the child to live a long and happy life. Ask your doctor or the hospital they can give you more info.
As of right now, there is no known cure for Prader-Willi Syndrome.
How can someone with Hunter's be defined as a mild case when he or she may be producing only 1% of the enzyme needed?
You mostly can't walk that good and you have bad un-normal teeth and a really big head. But most certainly, everyone who has morquio syndrome dies around at the age of 10 to 1…4. You can also have a bad chest and a bad spine but most people always have a strange squeaky or cracky voice.
I have suffered with RLS for many years, after many trials of different prescriptions, I am now using an antidepressant called Trazadone, and in the last 3 months I have only …suffered with my RLS once. I am sure this won't work for everyone but it did work for me, I used to suffer at least 4 times a week, leading to chronic insomnia.
The prognosis for recovery from TMJ is excellent for almost all patients. Most patients do not need any form of long-term treatment. Surgical procedures to treat TMJ are quite… successful.
TSS lasts as long as three weeks, and has a tendency to recur. About a third of the women who are treated for TSS have it again within six months. In addition, TSS can affect …the liver, kidneys, lungs, and other organs
There is currently no cure for it, although many doctors do think that a lot more people have it than there are currently known to be, as Ehlers-Danlos can sometimes be unnoti…ced for years, or even someone's whole life, even today. It can be managed- for example, I am a person with type II (also known of as the Classical type- I and II are NOT the same, and they shouldn't be treated as such), and so instead of wearing skirts and dresses with thin tights (or, shudder, nothing at all) underneath, I wear thicker leggings and don't climb trees. One can't do anything for the dislocations, and the internal types of EDS can't be helped. One can do family planning with a 50% chance (I think...) of it being correct, but if you are against it (can't blame you, I kinda am too), you can't prevent your kids from getting it and having them be yours genetically. People are currently working on finding a cure, although it is almost as close as some of the cures for cancer.
It is an in herited disesase there may be a high chance if inherid
There is no way to be absolutely positive that your child will not have Morquio's syndrome if both parents have the gene, but there are genetic screenings to help prevent havi…ng a child with Morquio's syndrome.