The goal of gene therapy is to restore normal amounts of aspartoacylase in the brain and nervous system and prevent the build-up of NAA and the symptoms of Canavan disease
Gene therapy is a significant medical breakthrough because it allows doctors to treat a disease before it becomes chronic or even reverse damage done by a chronic disease. It also allows for the treatment of diseases with no cure prior to gene therapy.
With the help of Gene therapy we can replace or supress the cancer gene
Gene Therapy cannot treat · Phenylketonuria · Gaucher Disease · Lesch-Nyhan Syndrome · Urea Cycle Disorders · Duchenne Muscular Dystrophy
Gene therapy is when DNA is used to treat a disease. The DNA is placed into the patient's cells to help heal them of the illness that is present.
It can be used to treat defects in somatic that is (body)or gametic (sperm or eggs) cell
Cosmetic gene therapy is a branch of medicine that deals with the maintenance and cure of the body disease.
Gene therapy effects children by helping to cure disease and to lengthen lives. Gene therapy can also be used to eliminate diseases that are inherited.
yes
In cystic fibrosis there is an inherited gene that you have that is causing it, so if gene therapy is used, you can replace the gene with the effected one
Identifying the faulty Gene. Identifying the faulty Gene that causes the disease.
Gene therapy is a method of treatment. It is specifically used to treat patients who are suffering from diseases due to defective genes. Essentially, the treatment involves researchers replacing the defective or faulty genes with a normal functioning gene. It involves: 1) Detection of gene 2)Determination & its role 3)Isolation & cloning 4)Introducing the gene by proper way. This is either germline gene therapy (done in germ cells) or somatic gene therapy (done in somatic cells).
There are a number of factors which have kept gene therapy from becoming an effective treatment for genetic disease. The viral rectors are the main problems which might make gene therapy to cause diseases.