How is genetic therapy used to treat genetic disorders?

Answer 1

Gene therapy is a method that aims to cure inherited diseases by providing the patient with correct copy of the defective gene.

There are four potential approaches to gene therapy:

1)

Addition of normal gene to replace the function of defective gene. This is gene replacement or

gene augmentation therapy.

2)

Replacing the defective gene with the correct gene. This is

Corrective gene therapy.

3)

Establishment of alternative pathways that bypass mutant genes function

4)

Change in regulation of normal or mutant genes

The first two are the basic approaches in gene therapy