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What is the desired outcome of gene therapy?
Gene therapy has the desired outcome of eradicating or curing diseases that are caused by a specific abnormality or mutation of a gene that is a killer. It is a developing science and slowly getting results.
How do gene splicing and gene therapy difffer?
Gene therapy usually seeks to replace a defective gene in a cell with the correct one using a vector for delivery, often a virus. The result is the transformed cells will product the correct protein. Protein therapy usually refers to injecting a functional protein into a patient to compensate for its absence.
Difference between gene therapy and protein therapy?
at the gene level gene therapy is done and at the the protein level protein therapy is done
Inserting working copies of a gene directly into the cells of a person with a genetic disorder is called what?
That process is called gene therapy. It involves inserting functional copies of a gene into the cells of a person with a genetic disorder to correct the genetic mutation causing the disorder.
What is the disavantage of geneterapy?
One disadvantage of gene therapy is the risk of triggering an immune response that could potentially harm the patient. Another concern is the difficulty in targeting the correct cells and ensuring the desired gene is integrated into the genome safely. Additionally, gene therapy can be expensive and may not be accessible to all individuals.
How could gene therapy be used to treat cancer?
With the help of Gene therapy we can replace or supress the cancer gene
When was gene therapy on allowed?
in 1989 us approve gene therapy exprement on human
In the SCID-X1 gene therapy trials what problem later surfaced in three of the patients?
In the SCID-X1 gene therapy trials, three patients developed leukemia as a result of the treatment. This was due to the unexpected activation of an oncogene during the insertion of the corrective gene into the patients' cells.
How does gene therapy effect children?
Gene therapy effects children by helping to cure disease and to lengthen lives. Gene therapy can also be used to eliminate diseases that are inherited.
What conditions can not be treated by gene therapy?
Many of the more commonly occurring disorders, including heart disease, diabetes, and high blood pressure, result from defects in multiple genes making them unlikely candidates for gene therapy using existing technologies.
How do you know if gene therapy is successful?
Gene therapy is considered successful if it achieves the desired therapeutic outcome, such as correcting a genetic mutation or restoring normal gene function. This can be evaluated through various methods, including monitoring changes in disease symptoms, measuring levels of the corrected gene or protein, and assessing the safety and efficacy of the treatment over time through clinical studies and patient monitoring. Regular follow-up assessments and monitoring are necessary to determine the long-term success of gene therapy.
Does gene therapy use RNA?
Yes, some gene therapy approaches use RNA molecules to deliver therapeutic genetic material into cells. This can be done using techniques such as RNA interference (RNAi) or RNA-based viral vectors to introduce desired genetic changes into a patient's cells.
