answersLogoWhite

0

Stargardt's disease

User Avatar

Wiki User

12y ago

What else can I help you with?

Related Questions

What is null allele?

A null allele is a mutant copy of gene that completely lacks that gene's normal function. This can be the result of the complete absence of the gene product (protein, RNA) at the molecular level, or the expression of a non-functional gene product. At the Phenotypic level, a null allele is indistinguishable from a deletion of the entire locus.


Gene feels a certain amount of towards Finny?

Gene feels jealousy towards Finny because he admires his athletic abilities and popularity, which Gene lacks. This jealousy leads Gene to sabotage Finny, ultimately causing a rift in their friendship.


What happens when there are changes in a gene?

The protein that the gene codes for changes or may even cease to be produced, depending on the change to the gene.


How has melanoma been treated with gene therapy?

involves introducing a gene with an anticancer protein called tumor necrosis factor (TNF) into test tube samples of the patient's own cancer cells, which are then reintroduced into the patient.


What happens to a gene for a protein that is not used much in the cell?

Nothing "happens" to it. When a gene is not actively being copied or expressed it is folded up and stored till it is needed again.


How is gene therapy used administered?

Gene therapy can be administered using viral vectors, which are genetically modified viruses that are used to deliver therapeutic genes into the patient's cells. These vectors can be injected directly into the target tissue or administered intravenously to reach various organs in the body. Another approach is ex vivo gene therapy, where cells are removed from the patient, genetically modified, and then infused back into the patient.


Who is benefiting from gene therapy?

Gene therapy is technique to treat a genetic disorder or cancer by inserting a gene to replace the defective one.It is now not widely in practice but this may be the future. The benefit is the patient can successfully attain the healthy gene and can be cured permanently.


Which of the following is the first step in gene therapy?

Identifying the faulty Gene. Identifying the faulty Gene that causes the disease.


What happens after a probe DNA is inserted into a patient's genome?

Once the probe DNA is inserted into a patient's genome, it will integrate with the host cell's DNA. The inserted DNA can potentially correct genetic mutations or provide therapeutic benefits by producing the desired protein. Monitoring the patient for any adverse effects or changes in gene expression is crucial post-insertion.


How gene therapy is used to treat genetic disorders?

Gene therapy is a method that aims to cure inherited diseases by providing the patient with correct copy of the defective gene. There are four potential approaches to gene therapy:1)Addition of normal gene to replace the function of defective gene. This is gene replacement orgene augmentation therapy.2)Replacing the defective gene with the correct gene. This isCorrective gene therapy.3)Establishment of alternative pathways that bypass mutant genes function4)Change in regulation of normal or mutant genesThe first two are the basic approaches in gene therapy


What happens when a steroid hormonoe binds to a receptor?

acts as a transcription factor and binds to DNA, activating a gene


What happens to Gene and Quackenbush as they are fighting?

Falling into the water