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Gene therapy is considered as a risky business as it has a chance of promoting cancer if the inserted DNA placed in a wrong place (locus). Gene therapy is aimed to cure genetic diseases by inserting DNA or gene as a drug in the tissue or cells. Viral vectors are the vehicles used for this purpose.
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What is the name for replacement of a defective gene with a healthy one?
gene therapy
What is one goal of gene therapy?
The goal of gene therapy is to cure a genetic disorder. Lets a gene is impaired by mutation and causing a disease. We can correct the gene by injecting DNA to the cells that have impaired gene. By this we can find out a permanent cure of that particular disease condition if it works properly.
What will be the likely benefits or risks involved in gene therapy?
no one knows and no one cares
How do gene splicing and gene therapy difffer?
Gene therapy usually seeks to replace a defective gene in a cell with the correct one using a vector for delivery, often a virus. The result is the transformed cells will product the correct protein. Protein therapy usually refers to injecting a functional protein into a patient to compensate for its absence.
Researchers hope to one day use gene therapy to?
Researchers hope that one day gene therapy can be used to cure epidemics like diabetes, cancer, obesity and a range of cardiac disorders D
How gene therapy might be used to treat cytic fibrosis?
Gene therapy for cystic fibrosis involves delivering a functional copy of the CFTR gene to affected cells in order to restore normal function of the protein. This can be achieved by using viral vectors to deliver the gene into the cells and allow it to produce normal CFTR protein. By correcting the underlying genetic defect, gene therapy holds promise for treating cystic fibrosis at the molecular level.
Where does one go to get gene therapy?
Gene therapy is an experimental treatment in which genetic material is introduced into a person's cells to cure disease. Because it is still experimental it is being done at research hospitals.
Explain what human gene therapy is?
If a person is lacking a gene that causes a disorder, for example diabetes, and a gene can be inserted into cells that require the gene, this would be gene therapy. Parkinson's disease and X-linked SCID are two that are be researched.
Where can one find synthetic biology?
Synthetic biology combines biology and engineering. One example is inserting a gene from one animal into the DNA of a different animal. This is useful for gene therapy applications.
What is the disavantage of geneterapy?
One disadvantage of gene therapy is the risk of triggering an immune response that could potentially harm the patient. Another concern is the difficulty in targeting the correct cells and ensuring the desired gene is integrated into the genome safely. Additionally, gene therapy can be expensive and may not be accessible to all individuals.
Involves placing a normal allele in a cell that has a mutation and hoping that the normal allele begins to function?
Gene therapy
How can one repair the p53 gene effectively?
Repairing the p53 gene effectively can be achieved through gene therapy techniques, such as using CRISPR-Cas9 to correct mutations in the gene. This approach involves precise editing of the gene to restore its normal function, which can help in treating diseases associated with p53 gene mutations.
